About Us

Accomplishments

RSZ TNC 2023 Highlights

The 2023 report highlights key achievements in our second year of operations including:

Clinical Trials
Launching a new gene therapy trial for girls with Rett Syndrome in partnership with Neurogene
Opening a Clinical Research Unit at 2 Brookline Place for clinical trial study visits

Faculty Members
Recruiting three brilliant new faculty members: Mandana Arbab, Jordan Farrell and Emily Osterweil

Events
Partnering with Global Genes and hosting a panel on the “Power of Partnering” at the Rare Advocacy Summit on Collaborative Research for Neurodevelopmental Disorders

Training Initiatives
Hosting a translational neuroscience fellowship program
Awarding 4 RSZ TNC Pilot Grants
Launching a new Clinical Psychology Advanced Graduate Practicum

2023 Annual Report

RSZ-Booklet-2023

RSZ TNC 2022 Highlights

The 2022 report highlights key achievements in our second year of operations including:

Symposium
Hosting an inaugural symposium entitled Gene Therapy for Pediatric Neurological Disorders and multiple community/science meetings  LEARN MORE >

New Advisory Council
Launching a Neuroscience Family Advisory Council research committee to ensure our clinical research includes the patient and family perspective LEARN MORE >

Faculty Members
Recruiting two new faculty members to lead RSZ TNC Cores: Dr. Jed Hubbs, Director of Medicinal Chemistry Core and Dr. Maya Chopra, Director of Translational Genomic Medicine Core

Pilot Grants
Awarding two new $100,000 RSZ TNC Pilot grants

Human Neuron Core
Sharing of standard operating procedures and tools developed by the Human Neuron Core

Publications
Publishing a seminal paper proposing a new framework for evaluation of disorders for development of gene therapy, GENE TARGET  READ THE PAPER >

RSZ TNC 2021 Highlights

Leadership Team
Key appointments: Executive Director, new Core Directors, Strategic Advisory Council.

Fellowship Awards
Two Translational Neuroscience Fellowships: the postdoctoral training program is two years in duration.

Pilot Grants
Four $100,000 awards to principal investigators for one-year RSZ TNC Pilot grants, with the possibility for a renewal the subsequent year.

Scientific/Family Conferences
We partner with patient advocacy groups to plan and conduct meetings between families and researchers. Learn more about RSZ TNC Events.

New Gene Therapy Core
Completed national search for two new faculty. Read more about our Core Facilities.

New Clinical and Research Space
The RSZ TNC Research Center at 2 Brookline Place opens in July 2023.

“Driving patient-centered research and care forward: A report on the Rosamund Stone Zander Translational Neuroscience Center.”

This December 2021 report summarizes the accomplishments achieved in our first year of operations.

RSZ_Booklet